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Spinal Muscular Atrophy

Latest News

FDA approved | Image Credit: © Frank H.-stock.adobe.com
March 30th 2026
FDA Approves High-Dose Nusinersen for SMA
By Maggie L. Shaw

In addition to the US, high-dose nusinersen (Spinraza; Biogen) is also approved in the European Union, Japan, and Switzerland.

Highlights from MDA 2025 | Image Credit: © AJMC
December 30th 2025

ICYMI: Highlights From MDA 2025

By Christina Mattina
FDA approval. | Image credit: aznan – stock.adobe.com
November 25th 2025

FDA Approves Gene Therapy Onasemnogene Abeparvovec for Broader SMA Population

By Hayden E. Klein
While the findings suggest that switching to onasemnogene abeparvovec after non–gene therapy treatments could be beneficial to patients with spinal muscular atrophy, it is not clear which patients may benefit the most from switching therapies. | Image credit: Rochu_2008 - stock.adobe.com
August 15th 2025

Switching to Gene Therapy After Nusinersen or Risdiplam May Benefit Patients With SMA

By Rose McNulty
FDA approval. | Image Credit: syahrir - stock.adobe.com
February 12th 2025

Risdiplam Tablet for Spinal Muscular Atrophy Receives FDA Approval

By Giuliana Grossi
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